Prophylaxis with granulocyte colony-stimulating factors (G-CSFs) reduces the incidence of febrile neutropenia in adults undergoing chemotherapy for solid tumours and lymphoma.[33]Wang L, Baser O, Kutikova L, et al. The impact of primary prophylaxis with granulocyte colony-stimulating factors on febrile neutropenia during chemotherapy: a systematic review and meta-analysis of randomized controlled trials. Support Care Cancer. 2015 Nov;23(11):3131-40.
https://link.springer.com/article/10.1007/s00520-015-2686-9
http://www.ncbi.nlm.nih.gov/pubmed/25821144?tool=bestpractice.com
[34]Renner P, Milazzo S, Liu JP, et al. Primary prophylactic colony-stimulating factors for the prevention of chemotherapy-induced febrile neutropenia in breast cancer patients. Cochrane Database Syst Rev. 2012 Oct 17;(10):CD007913.
https://www.cochranelibrary.com/cdsr/doi/10.1002/14651858.CD007913.pub2/full
http://www.ncbi.nlm.nih.gov/pubmed/23076939?tool=bestpractice.com
[35]Kuderer NMD. Impact of primary prophylaxis with granulocyte colony-stimulating factor on febrile neutropenia and mortality in adult cancer patients receiving chemotherapy: a systematic review. J Clin Oncol. 2007 Jul 20;25(21):3158-67.
http://www.ncbi.nlm.nih.gov/pubmed/17634496?tool=bestpractice.com
[36]Cooper KL, Madan J, Whyte S, et al. Granulocyte colony-stimulating factors for febrile neutropenia prophylaxis following chemotherapy: systematic review and meta-analysis. BMC Cancer. 2011 Sep 23;11:404.
https://bmccancer.biomedcentral.com/articles/10.1186/1471-2407-11-404
http://www.ncbi.nlm.nih.gov/pubmed/21943360?tool=bestpractice.com
Prophylactic use of G-CSF is recommended in patients:[23]Lyman GH, Abella E, Pettengell R. Risk factors for febrile neutropenia among patients with cancer receiving chemotherapy: a systematic review. Crit Rev Oncol Hematol. 2014 Jun;90(3):190-9.
http://www.ncbi.nlm.nih.gov/pubmed/24434034?tool=bestpractice.com
[37]National Comprehensive Cancer Network. NCCN clinical practice guidelines in oncology: hematopoietic growth factors [internet publication].
https://www.nccn.org/guidelines/category_3
[38]Smith TJ, Bohlke K, Lyman GH, et al. Recommendations for the use of WBC growth factors: American Society of Clinical Oncology clinical practice guideline update. J Clin Oncol. 2015 Oct 1;33(28):3199-212.
http://ascopubs.org/doi/full/10.1200/JCO.2015.62.3488
http://www.ncbi.nlm.nih.gov/pubmed/26169616?tool=bestpractice.com
[39]Aapro MS, Bohlius J, Cameron DA, et al; European Organisation for Research and Treatment of Cancer. 2010 update of EORTC guidelines for the use of granulocyte-colony stimulating factor to reduce the incidence of chemotherapy-induced febrile neutropenia in adult patients with lymphoproliferative disorders and solid tumours. Eur J Cancer. 2011 Jan;47(1):8-32.
http://www.ncbi.nlm.nih.gov/pubmed/21095116?tool=bestpractice.com
at high risk (>20%) for febrile neutropenia, or
at intermediate risk (10% to 20%) for febrile neutropenia who have ≥1 risk factor (i.e., age >65 years; prior chemotherapy; persistent neutropenia; prior radiotherapy; recent surgery; bone marrow involvement [by tumour]; liver dysfunction; renal dysfunction).
G-CSFs are not routinely recommended in patients at low risk (<10%) for febrile neutropenia, but may be considered (based on clinical judgment) in those who have two or more risk factors (i.e., age >65 years; prior chemotherapy; persistent neutropenia; prior radiotherapy; recent surgery; bone marrow involvement [by tumour] liver dysfunction; renal dysfunction).[23]Lyman GH, Abella E, Pettengell R. Risk factors for febrile neutropenia among patients with cancer receiving chemotherapy: a systematic review. Crit Rev Oncol Hematol. 2014 Jun;90(3):190-9.
http://www.ncbi.nlm.nih.gov/pubmed/24434034?tool=bestpractice.com
[37]National Comprehensive Cancer Network. NCCN clinical practice guidelines in oncology: hematopoietic growth factors [internet publication].
https://www.nccn.org/guidelines/category_3
If a patient developed febrile neutropenia during a prior cycle of chemotherapy and G-CSF prophylaxis was not used, then G-CSF prophylaxis should be considered for use with subsequent cycles of chemotherapy.[37]National Comprehensive Cancer Network. NCCN clinical practice guidelines in oncology: hematopoietic growth factors [internet publication].
https://www.nccn.org/guidelines/category_3
[38]Smith TJ, Bohlke K, Lyman GH, et al. Recommendations for the use of WBC growth factors: American Society of Clinical Oncology clinical practice guideline update. J Clin Oncol. 2015 Oct 1;33(28):3199-212.
http://ascopubs.org/doi/full/10.1200/JCO.2015.62.3488
http://www.ncbi.nlm.nih.gov/pubmed/26169616?tool=bestpractice.com
[39]Aapro MS, Bohlius J, Cameron DA, et al; European Organisation for Research and Treatment of Cancer. 2010 update of EORTC guidelines for the use of granulocyte-colony stimulating factor to reduce the incidence of chemotherapy-induced febrile neutropenia in adult patients with lymphoproliferative disorders and solid tumours. Eur J Cancer. 2011 Jan;47(1):8-32.
http://www.ncbi.nlm.nih.gov/pubmed/21095116?tool=bestpractice.com
Risk assessment for febrile neutropenia should be carried out after each cycle of chemotherapy.
Biosimilar formulations of G-CSF, and long-acting formulations (such as lipegfilgrastim, eflapegrastim, and efbemalenograstim alfa) are approved in some countries for chemotherapy-induced febrile neutropenia prophylaxis. Long-acting formulations may offer clinical benefits compared with short-acting G-CSFs, such as filgrastim.[40]Bond TC, Szabo E, Gabriel S, et al. Meta-analysis and indirect treatment comparison of lipegfilgrastim with pegfilgrastim and filgrastim for the reduction of chemotherapy-induced neutropenia-related events. J Oncol Pharm Pract. 2018 Sep;24(6):412-23.
https://journals.sagepub.com/doi/full/10.1177/1078155217714859
http://www.ncbi.nlm.nih.gov/pubmed/28614980?tool=bestpractice.com
[41]Pfeil AM, Allcott K, Pettengell R, et al. Efficacy, effectiveness and safety of long-acting granulocyte colony-stimulating factors for prophylaxis of chemotherapy-induced neutropenia in patients with cancer: a systematic review. Support Care Cancer. 2015 Feb;23(2):525-45.
http://www.ncbi.nlm.nih.gov/pubmed/25284721?tool=bestpractice.com
[42]Schwartzberg LS, Bhat G, Peguero J, et al. Eflapegrastim, a long-acting granulocyte-colony stimulating factor for the management of chemotherapy-induced neutropenia: results of a phase III trial. Oncologist. 2020 Aug;25(8):e1233-41.
https://academic.oup.com/oncolo/article/25/8/e1233/6443672
http://www.ncbi.nlm.nih.gov/pubmed/32476162?tool=bestpractice.com
[43]Cobb PW, Moon YW, Mezei K, et al. A comparison of eflapegrastim to pegfilgrastim in the management of chemotherapy-induced neutropenia in patients with early-stage breast cancer undergoing cytotoxic chemotherapy (RECOVER): a phase 3 study. Cancer Med. 2020 Sep;9(17):6234-43.
https://onlinelibrary.wiley.com/doi/10.1002/cam4.3227
http://www.ncbi.nlm.nih.gov/pubmed/32687266?tool=bestpractice.com
One systematic review concluded that more clinical trials are necessary to assess the benefits and harms of CSFs compared with antibiotics for the prevention of infection in cancer patients of all ages receiving chemotherapy.[44]Skoetz N, Bohlius J, Engert A, et al. Prophylactic antibiotics or G(M)-CSF for the prevention of infections and improvement of survival in cancer patients receiving myelotoxic chemotherapy. Cochrane Database Syst Rev. 2015 Dec 21;(12):CD007107.
https://www.cochranelibrary.com/cdsr/doi/10.1002/14651858.CD007107.pub3/full
http://www.ncbi.nlm.nih.gov/pubmed/26687844?tool=bestpractice.com
Antibacterial prophylaxis
Joint ASCO and Infectious Diseases Society of America (IDSA) guidelines recommend antibiotic prophylaxis with a fluoroquinolone for patients at high risk for febrile neutropenia or profound, protracted (>7 days) neutropenia, such as patients with acute myeloid leukaemia, myelodysplastic syndromes, or haematopoietic stem-cell transplantation treated with myeloablative conditioning regimens.[45]Taplitz RA, Kennedy EB, Bow EJ, et al. Antimicrobial prophylaxis for adult patients with cancer-related immunosuppression: ASCO and IDSA clinical practice guideline update. J Clin Oncol. 2018 Oct;36(30):3043-54.
http://ascopubs.org/doi/full/10.1200/JCO.18.00374
http://www.ncbi.nlm.nih.gov/pubmed/30179565?tool=bestpractice.com
Fluoroquinolone prophylaxis in high-risk patients requires a careful risk-benefit assessment over time, accounting for local and regional rates of fluoroquinolone resistance and other consequences of prophylactic broad-spectrum antibiotic use.[46]Mikulska M, Averbuch D, Tissot F, et al. Fluoroquinolone prophylaxis in haematological cancer patients with neutropenia: ECIL critical appraisal of previous guidelines. J Infect. 2018 Jan;76(1):20-37.
http://www.ncbi.nlm.nih.gov/pubmed/29079323?tool=bestpractice.com
Patients receiving prophylaxis should be closely monitored for the emergence of resistant organisms.[1]Freifeld AG, Bow EJ, Sepkowitz KA, et al. Clinical practice guideline for the use of antimicrobial agents in neutropenic patients with cancer: 2010 update by the Infectious Diseases Society of America. Clin Infect Dis. 2011 Feb 15;52(4):e56-93.
https://academic.oup.com/cid/article/52/4/e56/382256
http://www.ncbi.nlm.nih.gov/pubmed/21258094?tool=bestpractice.com
Antibiotic prophylaxis is not routinely recommended for patients with solid tumours.[45]Taplitz RA, Kennedy EB, Bow EJ, et al. Antimicrobial prophylaxis for adult patients with cancer-related immunosuppression: ASCO and IDSA clinical practice guideline update. J Clin Oncol. 2018 Oct;36(30):3043-54.
http://ascopubs.org/doi/full/10.1200/JCO.18.00374
http://www.ncbi.nlm.nih.gov/pubmed/30179565?tool=bestpractice.com
Antifungal prophylaxis
Prophylaxis using an oral azole or a parenteral echinocandin is recommended for patients at risk for profound and prolonged neutropenia; for example, those with acute myeloid leukaemia or myelodysplastic syndromes, or those undergoing haematopoietic stem-cell transplantation.[45]Taplitz RA, Kennedy EB, Bow EJ, et al. Antimicrobial prophylaxis for adult patients with cancer-related immunosuppression: ASCO and IDSA clinical practice guideline update. J Clin Oncol. 2018 Oct;36(30):3043-54.
http://ascopubs.org/doi/full/10.1200/JCO.18.00374
http://www.ncbi.nlm.nih.gov/pubmed/30179565?tool=bestpractice.com
A mould-active azole antifungal (e.g., voriconazole, posaconazole, isavuconazole) is recommended for prophylaxis where the risk of invasive aspergillosis is >6%, such as in patients with acute myeloid leukaemia or myelodysplastic syndromes during the neutropenic period associated with chemotherapy.[45]Taplitz RA, Kennedy EB, Bow EJ, et al. Antimicrobial prophylaxis for adult patients with cancer-related immunosuppression: ASCO and IDSA clinical practice guideline update. J Clin Oncol. 2018 Oct;36(30):3043-54.
http://ascopubs.org/doi/full/10.1200/JCO.18.00374
http://www.ncbi.nlm.nih.gov/pubmed/30179565?tool=bestpractice.com
For standard-risk autologous and allogeneic haematopoietic stem-cell transplant recipients, use of fluconazole prophylaxis during neutropenia is the conventional approach, with use of mould-active azole prophylaxis typically reserved for those patients with increased risk for mould infection or prior history of mould infection (i.e., secondary prophylaxis).[1]Freifeld AG, Bow EJ, Sepkowitz KA, et al. Clinical practice guideline for the use of antimicrobial agents in neutropenic patients with cancer: 2010 update by the Infectious Diseases Society of America. Clin Infect Dis. 2011 Feb 15;52(4):e56-93.
https://academic.oup.com/cid/article/52/4/e56/382256
http://www.ncbi.nlm.nih.gov/pubmed/21258094?tool=bestpractice.com
[45]Taplitz RA, Kennedy EB, Bow EJ, et al. Antimicrobial prophylaxis for adult patients with cancer-related immunosuppression: ASCO and IDSA clinical practice guideline update. J Clin Oncol. 2018 Oct;36(30):3043-54.
http://ascopubs.org/doi/full/10.1200/JCO.18.00374
http://www.ncbi.nlm.nih.gov/pubmed/30179565?tool=bestpractice.com
[47]Groll AH, Pana D, Lanternier F, et al. 8th European Conference on Infections in Leukaemia: 2020 guidelines for the diagnosis, prevention, and treatment of invasive fungal diseases in paediatric patients with cancer or post-haematopoietic cell transplantation. Lancet Oncol. 2021 Jun;22(6):e254-69.
http://www.ncbi.nlm.nih.gov/pubmed/33811813?tool=bestpractice.com
Risk of invasive mould infection is increased in patients with corticosteroid-requiring graft-versus-host disease following allogeneic haematopoietic stem-cell transplantation, and a mould-active azole (e.g., posaconazole) should be strongly considered in this context.[45]Taplitz RA, Kennedy EB, Bow EJ, et al. Antimicrobial prophylaxis for adult patients with cancer-related immunosuppression: ASCO and IDSA clinical practice guideline update. J Clin Oncol. 2018 Oct;36(30):3043-54.
http://ascopubs.org/doi/full/10.1200/JCO.18.00374
http://www.ncbi.nlm.nih.gov/pubmed/30179565?tool=bestpractice.com
Mould-active azoles are associated with adverse effects, toxicity, and drug-drug interactions that merit careful consideration.
Antifungal prophylaxis is not routinely recommended for patients with solid tumours.[45]Taplitz RA, Kennedy EB, Bow EJ, et al. Antimicrobial prophylaxis for adult patients with cancer-related immunosuppression: ASCO and IDSA clinical practice guideline update. J Clin Oncol. 2018 Oct;36(30):3043-54.
http://ascopubs.org/doi/full/10.1200/JCO.18.00374
http://www.ncbi.nlm.nih.gov/pubmed/30179565?tool=bestpractice.com